Delivering extraordinary. Empowering ordinary.

We’re developing novel oral medicines for rare diseases to help patients take part in the everyday activities they enjoy.

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Structure-guided Drug Design

We combine traditional cell biology with medicinal chemistry to build synthetic compounds that bind to specific protein targets to fight disease.

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Building a Rare Disease Drug Portfolio

We are developing a pipeline of oral drugs for rare diseases.

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Join Our Team

We are a collection of passionate individuals united by a commitment to scientific excellence and an unwavering focus on the needs of patients.